Hello @betsy7 - I combined your discussion with an existing discussion titled "Limb girdle muscular dystrophy" - https://connect.mayoclinic.org/discussion/limb-girdle-muscular-dystrophy/ to meet @mmbamfra0019, @ditamontoya and @dbwhitted.

@betsy7, have you been denied a particular treatment or trial and that is why you are inquiring about the right to try act? For anyone wondering, the Right to Try Act is as follows: https://www.fda.gov/media/133864/download#:~:text=Right%20to%20Try%20is%20one,and%20Drug%20Administration%20(FDA).